Patrick Aubourg Comments on Gene Therapy Success for Adrenoleukodystrophy (ALD)


In this video, Patrick Aubourg, MD of INSERM in France, and the co-author of the gene therapy paper published in the Journal Science, reveals their successful results treating 2 young boys with adrenoleukodystrophy (ALD). ALD is the disease highlighted in the movie “Lorenzo’s Oil.” The Stop ALD Foundation played a pivotal role in making this trail happen.
Video Rating: 5 / 5

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One Response to Patrick Aubourg Comments on Gene Therapy Success for Adrenoleukodystrophy (ALD)

  1. pewee912 says:

    My son was diognosed with ALD what can i do please help!!!maldonado_lina@yahoo.com

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